Molecular Genetics and Metabolism Reports
ISSN: 2214-4269
Publisher: Elsevier
Publications (2)
Response to Gurevich and colleagues: The effect of enzyme replacement therapy on clinical outcomes in male patients with Fabry disease: a systematic literature review by a European panel of experts (2019)
Germain DP, Falissard B, Hilz MJ, Spada M, Wanner C, Elliott PM
Journal article, Letter
The effect of enzyme replacement therapy on clinical outcomes in male patients with Fabry disease: A systematic literature review by a European panel of experts. (2019)
Germain DP, Elliott PM, Falissard B, Fomin VV, Hilz MJ, Jovanovic A, Kantola I, et al.
Journal article, Review article